# One Genetic Edit, Lifetime Protection: Rockefeller Team Programs Immune Cells as Drug Factories

- slug: one-genetic-edit-lifetime-protection-rockefeller-team-programs-immune-cells-as-drug-factories
- date: 2026-04-17
- category: Biotech & Life Sciences

Children with severe genetic metabolic disorders spend their lives on IV protein infusions. A single CRISPR edit to blood stem cells let mice produce their own therapeutic proteins for months, raising the prospect of a one-time treatment replacing lifetime enzyme therapy.

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